Skip to Main Content (Press Enter)
×
Home
People
Outputs
Organizations
Expertise & Skills
IT
EN
☰
UNI-FIND
|
UNI-FIND
cnr.it
IT
EN
×
Home
People
Outputs
Organizations
Expertise & Skills
☰
Outputs
MOLECULAR THERAPY (ONLINE)
Journal
Identifier:
E214677
ISSN:
1525-0024
Overview
Overview
Outputs (9)
A chaperone enhances blood ?-glucosidase activity in Pompe disease patients treated with enzyme replacement therapy.
Academic Article
An optimized SpCas9 high-fidelity variant for direct protein delivery
Academic Article
Cell-Specific Transcriptional Regulatory Domains Attract y-Retroviral Integration in the Human Genome
Academic Article
Chromosome Transplantation: A Possible Approach to Treat Human X-linked Disorders
Academic Article
Mucosal delivery of a vectored RSV vaccine is safe and elicits protective immunity in rodents and nonhuman primates
Academic Article
Pharmacological enhancement of alpha-glucosidase by the allosteric chaperone N-acetylcysteine
Academic Article
Smooth muscle cell-targeted RNA aptamer inhibits neointimal formation
Academic Article
Successful Preclinical Development of Gene Therapy for Recombinase-Activating Gene-1-Deficient SCID
Academic Article
Therapeutic Potential of Immunoproteasome Inhibition in Duchenne Muscular Dystrophy
Academic Article
No Results Found
