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MOLECULAR THERAPY (ONLINE)
Rivista
Codice:
E214677
ISSN:
1525-0024
Dati Generali
Dati Generali
Pubblicazioni (9)
A chaperone enhances blood ?-glucosidase activity in Pompe disease patients treated with enzyme replacement therapy.
Articolo
An optimized SpCas9 high-fidelity variant for direct protein delivery
Articolo
Cell-Specific Transcriptional Regulatory Domains Attract y-Retroviral Integration in the Human Genome
Articolo
Chromosome Transplantation: A Possible Approach to Treat Human X-linked Disorders
Articolo
Mucosal delivery of a vectored RSV vaccine is safe and elicits protective immunity in rodents and nonhuman primates
Articolo
Pharmacological enhancement of alpha-glucosidase by the allosteric chaperone N-acetylcysteine
Articolo
Smooth muscle cell-targeted RNA aptamer inhibits neointimal formation
Articolo
Successful Preclinical Development of Gene Therapy for Recombinase-Activating Gene-1-Deficient SCID
Articolo
Therapeutic Potential of Immunoproteasome Inhibition in Duchenne Muscular Dystrophy
Articolo
No Results Found
