Long-term evaluation of respiratory outcomes in patients with late onset Pompe disease under enzyme replacement therapy: the role of postural drop and its impact on quality of life
Abstract
Publication Date:
2021
abstract:
Monitoraggio longitudinale di pazienti con pazienti con malattia di Pompe
Iris type:
01.05 Abstract in rivista
Keywords:
respiratory evaluation; Pompe disease; Enzyme replacement therapy
List of contributors:
Crescimanno, Grazia
Published in: